Live Science's health channel editor makes predictions about the medical breakthroughs and public health shifts to come in ...

Matthew Herper covers medical innovation — both its promise and its perils. It has been a tough year for medicine. The U.S.

Beam Therapeutics BEAM is engaged in developing investigational gene therapy candidates that are currently in ...

Now, Musunuru and colleagues are preparing a master clinical protocol to study a CRISPR therapy that's mostly the same as the one they used to treat baby KJ, except they plan to swap out the gene ...

A small group of volunteers will receive multiple injections of the experimental treatments next month, says Unlimited Bio.

In the past three years, gene therapy has reshaped what's possible in hemophilia treatment for patients 18 and older. But a key question remains: How soon will these advances reach children?

Antibody-based therapies are used to treat numerous diseases, from cancer to rheumatic disorders and multiple sclerosis.

Today, after receiving a gene therapy developed at the University of California San Diego, Natalie is thriving at 34 years old. She’s built a career as a social worker, is happily married and recently ...

A new class of drugs is saving the lives of children who once had no hope. These high-tech medicines can replace defective genes. But there's a catch. Many cost millions of dollars for a single dose.

LAKELAND, Fla. (WFLA) — This holiday season, a Lakeland family is wishing to go to North Carolina. It is not for a vacation, but instead an intensive, specialized therapy for a toddler with an “ultra ...

CORONA, Calif. (KABC) -- A teenage girl is alive thanks to an experimental gene therapy treatment created at UCLA. She was born with a rare genetic disorder, so any common infection could've killed ...

A genetic disorder that leads to bleeding episodes and life-threatening infections has a new FDA approved treatment, a regulatory decision that marks two notable firsts — the first gene therapy for ...